Enzyme replacement therapy for Gaucher Disease: the only experience in Malaysia.
نویسندگان
چکیده
Gaucher Disease may now be treated with enzyme replacement therapy (ERT) or bone marrow transplantation (BMT). Both have their advantages and disadvantages. Results with BMT are curative when successful but limited by the scarcity of an appropriate donor. ERT offers very good relief of symptoms but treatment is lifelong and cost of treatment exorbitant. Patients in developing countries are particularly disadvantaged and management remains a dilemma for both doctor and patient.
منابع مشابه
P-111: An Attempt to Facilitate the Production of Transgenic Mouse As A Model for Gene Therapy of Gaucher Disease
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ورودعنوان ژورنال:
- The Medical journal of Malaysia
دوره 57 3 شماره
صفحات -
تاریخ انتشار 2002